News

Orphan Pleaded to Be Adopted in 2013. Now He Shares 'Trauma' He Endured in Foster Care — and Finding Love with a Family
"Remember your past, but don't live in your past," Davion Only Going was once told. "Because if you live in your past, your ...
Prices for new US drugs doubled in 4 years as focus on rare disease grows
U.S. President Donald Trump's trade negotiators are pushing the EU to make unilateral tariff reductions on U.S. goods, saying ...
Rare Disease Patients Await Congressional Action on Life-Saving Treatments
President Trump recently signed a wide-ranging executive order urging Congress to amend a crucial provision of a Biden-era ...
BioSpace1d
Changes to IRA Pill Penalty Conspicuously Absent as Congress Narrowly Passes Trump’s Tax Bill
The "One Big Beautiful Bill Act" includes negotiation exemptions for orphan drugs approved to treat more than one rare ...
Bleeding Cool2d
James Stokoe's Orphan And The Five Beasts is Back in September
James Stokoe returns with Orphan and the Five Beasts: Bath of Blood, hitting comic shops in September 2025. Orphan Mo ...
Business Wire11d
Cure Rare Disease Receives Orphan Drug Designation from FDA for Investigational Therapy Targeting Spinocerebellar Ataxia Type 3 (SCA3)
“Receiving Orphan Drug Designation for our SCA3 program is an important milestone and a validation of our mission to deliver life-saving therapies to patients with ultra-rare and rare diseases ...
Swedish Orphan Biovitrum: Haematology Focus Seems To Be Paying Off
BIOVF shifts to a strategic portfolio emphasizing Haematology, driving strong revenue growth. Key catalysts in 2025.
Healio4d
FDA nudges development of drug to prevent necrotizing enterocolitis
The FDA recently granted orphan drug and rare pediatric disease designations to Infinant Health for a live biotherapeutic ...
Eos8d
Scientists Map Where Orphan Wells Pose Threats to Aquifers
A new study from the U.S. Geological Survey finds that groundwater in Appalachia, the Gulf Coast, and California is ...